Goals, Mission & Vision
Our Mission
ROAR unites patients, caregivers, clinicians, and researchers to learn how organic acidemias change over time and to identify what treatments and supports work best. By collecting high‑quality clinical, genetic, and patient‑reported data across many centers, we aim to guide better care today and enable better therapies for the future.
Our Vision
To improve the lives of people with organic acidemias by advancing understanding, strengthening clinical care, and supporting families across every stage of life.
Our Goals
Understand how organic acidemias progress across childhood and adulthood. Identify the most effective clinical practices to prevent crises and protect organ function. Strengthen support for feeding, growth, neurodevelopment, and quality of life. Build a research partnership with families and patient organizations. Create a foundation for future clinical trials and new therapies.